The Art of Decentralizing Pediatric Rare Disease Studies: Clinical Trials Suited for Daily Life

Pediatric rare disease trials combine rarity of disease with a restricted and geographically-dispersed population of vulnerable subjects for research, creating unique challenges for study design and execution. Recruitment is challenging, as patients, parents and caregivers need to juggle school schedules, work responsibilities and family obligations to accommodate study participation.

Incorporating decentralized clinical trial (DCT) strategies can help sponsors attract patients and increase access, enrollment and retention by limiting site visits and facilitating participation for those who might not otherwise be able — or willing — to travel to distant sites or specialized centers.

Join this webinar to learn:

• Challenges of conducting clinical research in pediatric rare diseases
• Potential applications of DCT strategies in pediatric rare disease studies
• Risks to applying DCT strategies in these clinical trials
• Key considerations when operationalizing pediatric rare disease studies with decentralized elements
• Future trends in decentralization for pediatric rare disease studies

Speakers

Betsy Reid, Senior Vice President, Pediatrics, Premier Research

Betsy Reid is responsible for providing the strategic direction for portfolio growth and operational excellence through direct leadership of the project management teams focused on executing decentralized studies and programs.

Betsy is a results-driven executive with a proven track record of developing and leading groups and organizations to increased profitability, productivity, and growth. She has a proven track record of success in driving execution of organizational strategy in support of operational excellence as well as in developing, negotiating, and implementing strategic alliances and partnerships to support strategy. Betsy achieves these goals by developing and implementing a clear business strategy, building committed, motivated and successful teams, and leading through change to optimal results for the organization.

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Dr. Adam Bloomfield, MD, FAAP, Executive Director, Medical Affairs, Rare Diseases and Pediatrics, Premier Research

Dr. Adam Bloomfield oversees the Rare Diseases and Pediatrics Medical Affairs team at Premier Research. He brings to Premier extensive US and global experience in medical affairs leadership and clinical development strategy from his previous work at AstraZeneca, Sobi, and Moderna. In his current role, he provides medical monitoring oversight, therapeutic knowledge to study programs, and supports business development and consulting activities in the fields of Rare Disease and Pediatrics.  A pediatrician by training, Dr. Bloomfield has over fifteen years of clinical experience treating thousands of patients and brings a patient-centric perspective to research programs.

Dr. Bloomfield completed his pediatric residency training at New York University Medical Center. He holds a doctor of medicine degree from Rutgers New Jersey Medical School and a bachelor of science degree in mathematics from the University of Michigan – Ann Arbor. He is a fellow of the American Academy of Pediatrics and board certified by the American Board of Pediatrics.

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